TY - BOOK AU - Thoene,Jess G. TI - Small molecule therapy for genetic disease SN - 9780521517812 (hbk.) U1 - 616.39042 PY - 2010/// CY - Cambridge PB - Cambridge University Press KW - Metabolism, Inborn errors of KW - Chemotherapy KW - Handbooks, manuals, etc KW - Gene therapy KW - Genetic disorders N1 - Includes bibliographical references and index ER -